PEDIATRIC NEUROTRANSMITTER DISEASE ASSOCIATION INC

Aromatic Amino Acid Decarboxylase (AADC)Deficiency is a Pediatric Neurotransmitter Disease…

AADC Gene Therapy is a treatment which is just around the corner and we desperately need your help to bring it to our suffering AADC deficient children throughout the WORLD!

AAV-AADC was originally a gene vector created for Parkinson ’s disease by Professor Krystof Bankiewicz (Prof. B) in the USA...but as luck would have it, this is also a treatment potentially suitable for AADC deficient children too. It has the capability to be life-changing and lead to impressive improvements even to the most disabled of our children.

We are raising funds to help Prof. B complete all the necessary safety regulatory requirements in order to bring this trial to life...

The Gene Therapy trial will be at the NIH and hopefully commence mid-year 2013.

Our target to raise is massive $50,000. But this is a fraction of the overall cost of the trial. The AADC Research Trust has already set aside $10,000 of its funds to this project and the PND and ALADD Foundation have still to announce their contributions.

PLEASE PLEASE give generously!

A GIGANTIC thank you from all our beautiful suffering children: Sydney, Delaini, Swathi, Jillian, Marlie, Luis, Gavin, Sydney Claire, Riley, Marissa, Jake, Ted, Marcus, Mohanad, Muiad, Vincent, Romain, Zain, Haia, Nathan, Sofia, Satoshi, Lily, Lavinia, Lynn, Joyce, Tehila, Ryder, Daniel, Aniya, Romanja, Hulya, Aimar, Peeter, Sellina and Emily

Definition of 'PND'
Pediatric Neurotransmitter Disease is an umbrella term for genetic disorders that affect the synthesis, metabolism and catabolism of neurotransmitters in
children.

These inborn errors of metabolism affect the central nervous system in children and if left untreated can lead to severely compromised neurological function.

The symptoms of some pediatric neurotransmitter diseases can be completely treated whereas in other pediatric neurotransmitter diseases, such as AADC, treatment
can only sometimes improve quality of life.

Visit:
www.aadcresearch.org or www.pndassoc.org to learn more about these devastating disorders.

Contact lisa@aadcresearch.org for more information about how you can help us raise funds!